Rare diseases affect one in 10 people.

CMT4J is a rare, progressive, neurological disease similar to ALS.

CureCMT4J is a non-profit created by parents of Talia, a teenage girl with severe, early-onset CMT4J. CureCMT4J is the only entity working toward a treatment or cure for this deadly disease. YOU can help us to get there. 

Chase the Butterfly is BACK!

Join us on Sunday, May 19th at 10 a.m. for face paint, music, games, food from Riverview Pizza and Whoopie Wagon, and a run through beautiful Bradley Palmer State Park! Let’s bring the community together for the fifth annual run/walk/roll!

OF OUR $2,200,000 GOAL


Our researchers working together from The Jackson Laboratory, UT Southwestern, and University of Michigan have shown great success in using gene therapy to treat CMT4J mouse models! We’re working hard on getting it into a clinical trial! 

Gene Therapy

Drug Repurposing

To learn more about our research visit our Research Pathway page

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