Rare diseases affect one in 10 people.

CMT4J is a rare, progressive, neurological disease similar to ALS.

CureCMT4J is a non-profit created by parents of Talia, a teenage girl with severe, early-onset CMT4J. CureCMT4J is the only entity working toward a treatment or cure for this deadly disease. YOU can help us to get there. 

Third Chase the Butterfly was a huge success!
Sarah Eliot organized the third running of our Chase the Butterfly 3-mile run. After a two-year hiatus due to Covid, Sarah’s hard work raised nearly $10,000 for CureCMT4J! Thank you to Sarah and her parents, Kate and Pete, and all of our sponsors for their never-ending support and kindness!

$1,415,529
OF OUR $2,200,000 GOAL

CURECMT4J IS DRIVING RESEARCH TOWARD TREATMENTS

Our researchers working together from The Jackson Laboratory, UT Southwestern, and University of Michigan have shown great success in using gene therapy to treat CMT4J mouse models! We’re working hard on getting it into a clinical trial! 

Gene Therapy

Drug Repurposing

To learn more about our research visit our Research Pathway page

Help us spread the word!

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