Rare Disease by the Numbers

Rare diseases are surprisingly common.

Rare disease by the numbers:

  • Over 10,000 rare diseases exist
  • One in 10 Americans is affected by a rare disease
  • 80% of rare diseases involve a faulty gene, providing ideal opportunities for gene therapy
  • 30 million people in the U.S. and 350 million people worldwide have a rare disease
  • 50% of rare diseases affect children, causing death or debilitating illness at a young age
  • Rare diseases affect more people than AIDS and cancer-related illness combined
  • Only 5% of all rare diseases currently have a treatment or cure

WE NEED YOU!

Because rare diseases are small individually, they receive little funding for research and the development of treatments. Patients, parents and rare disease patient communities are often the only driving force behind therapeutic development
DONATE or reach out to find how YOU can help today!